En un artículo publicado en "The New England Journal of Medicine", médicos de la Universidad de Duke (Estados Unidos) explican cómo trataron a 20 niños con síndrome de Hurler destruyendo primero su médula ósea e inyectando posteriormente sangre de cordón umbilical de donantes no emparentados.
El procedimiento funcionó en 17 niños. Todos éstos comenzaron a producir la enzima que degrada los mucopolisacáridos y empezaron a experimentar un crecimiento normal. Los otros 3 pacientes fallecieron.
Webs Relacionadas
Duke University
http://www.duke.edu/
New England Journal of Medicine
http://content.nejm.org/
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Publicado el 25 de mayo de 2004
Sindrome de Hurler
Sangre de cordón umbilical para el síndrome de Hurler
Sangre de cordón umbilical puede ser utilizada para tratar con éxito a niños con síndrome de Hurler, enfermedad hereditaria a menudo mortal causada por la acumulación de sustancias que contienen azúcar en el cránea, cara, cerebro y corazón.
En un artículo publicado en "The New England Journal of Medicine", médicos de la Universidad de Duke (Estados Unidos) explican cómo trataron a 20 niños con síndrome de Hurler destruyendo primero su médula ósea e inyectando posteriormente sangre de cordón umbilical de donantes no emparentados.
El procedimiento funcionó en 17 niños. Todos éstos comenzaron a producir la enzima que degrada los mucopolisacáridos y empezaron a experimentar un crecimiento normal. Los otros 3 pacientes fallecieron.
Webs Relacionadas
Duke University
http://www.duke.edu/
New England Journal of Medicine
http://content.nejm.org/